CRISPR Therapeutics AG
CRSPintermediaryCRISPR Therapeutics made history with the first FDA-approved CRISPR gene-editing therapy, Casgevy, for sickle cell disease. Co-founded by Nobel laureate Emmanuelle Charpentier, the company is leveraging its gene-editing platform across hematology, oncology (allogeneic CAR-T), and in vivo applications to create potentially curative one-time treatments.
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Segmentzusammensetzung und Hauptkunden
Produktdetails
First CRISPR-based gene therapy approved for sickle cell disease and beta-thalassemia
Off-the-shelf CRISPR-edited CAR-T cell therapies for blood cancers
Next-gen lipid nanoparticle-delivered CRISPR for liver and other organs
Lieferkettenbeziehungen
Wettbewerber
Makro- und Marktkontext
GLP-1 메가트렌드 + AI 신약개발 + 저평가 바이오 기관 매집
GLP-1 시장 규모 (2030E)
mRNA 암백신 임상 성공률
AI 신약개발 단계
PFE/MRNA 52주 변화
Nächste Katalysatoren
Aktuelle Nachrichten
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Unternehmensinformationen
Sektorübersicht — 제약 / 바이오
SektornachrichtenGLP-1 메가트렌드 + AI 신약개발 + 저평가 바이오 기관 매집
GLP-1 시장 규모 (2030E)
mRNA 암백신 임상 성공률
AI 신약개발 단계
PFE/MRNA 52주 변화
Hauptthemen
- •Mounjaro/Wegovy — 비만·당뇨 넘어 심혈관·신장·NASH 적응증 확대
- •Moderna mRNA-4157 암백신 — 흑색종 49% 재발 감소 (NEJM)
- •REGN dupilumab 다적응증 확대 → 10조+ 매출 가시성
Nächste Katalysatoren
- ◆LLY Orforglipron(경구용 GLP-1) 3상 결과 (2026.Q2)
- ◆MRNA 암백신 FDA BLA 제출 예정